Long Term Follow-up Study of Type-1 Gaucher Subjects Post FLT201 Dose (GALILEO-2)
75 patients around the world
Available in Brazil, United States
Freeline Therapeutics
1Research sites
75Patients around the world
This study is for people with
Gaucher disease
Gaucher disease type 1
Requirements for the patient
From 18 Years
All Gender
Medical requirements
Participants who have previously received FLT201 including those who may have required recommencement or initiation of ERT/substrate reduction therapy.
Participants able to give full informed consent and able to comply with all requirements of the trial.
Sites
Hospital de Clínicas de Porto Alegre
Rua Ramiro Barcelos, 2350, Av. Protásio Alves, 211 - Santa Cecília, Porto Alegre - RS, 90035-903